The baby, KJ Muldoon of Clifton Heights, Penn., is one of 350 million people worldwide with rare diseases, most of which are ...

The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...

A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...

KJ Muldoon became the first patient to undergo personalized CRISPR treatment, a therapy that found the one uniquely mutated gene out of 20,000 in his little body, and fixed it.

A big breakthrough is being hailed in the world of gene editing, with the first custom-designed treatment using CRISPR ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a ...

Ask scientists what gene editing tool is most needed to advance gene therapy, and they'd probably describe a system that's now close to realization in the labs of Samuel Sternberg at Columbia ...