As GL-3 accumulates, it can cause mild to severe symptoms that may lead to serious complications, including heart attacks, strokes, and kidney failure. Fabry's disease is diagnosed more often in ...

Fabrazyme is used in adults and certain children to treat Fabry disease. This is a rare ... But if you have symptoms that are ongoing or bothersome, talk with your doctor or pharmacist.

Preliminary clinical data suggest that AL01211 stabilizes Fabry disease symptoms, including eGFR and proteinuria levels, and shows positive trends in pain reduction, quality of life, and global ...

Amicus Therapeutics’ first oral drug for the rare condition Fabry disease has been approved by the FDA, giving patients an alternative to conventional injected enzyme replacement therapy.